What is it?
RNA therapeutics focuses on the development of treatments based on ribonucleic acid (RNA), a molecule that plays a crucial role in the regulation of gene expression and cellular processes. RNA-based therapies can be used to modulate the expression of disease-causing genes, providing a targeted and potentially more effective approach to treating a wide range of conditions.
Why is it important?
RNA therapeutics offer a highly targeted approach to treating diseases by modulating the expression of specific genes, enabling personalized treatments based on a patient’s genetic profile. RNA-based therapies can be used to address the root cause of genetic disorders by correcting or compensating for disease-causing mutations, offering the potential for disease modification or cure. RNA therapeutics can target a wide range of disease-causing genes and pathways that are difficult to address with traditional small molecule drugs or antibodies, expanding the range of druggable targets and treatment options.
What industries will it impact?
Pharmaceutical and biotech, Genetic testing and diagnostics, Drug delivery and formulation, Healthcare.
Market players
GSK, Ionis Pharmaceuticals, Stoke Therapeutics, PepGen, Arrowhead Pharmaceuticals, Sirnaomics, Evox therapeutics, Wave Life Sciences